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Federico Mingozzi

9PUBLICATIONS

69CO-AUTHORS

Gene and molecular therapyNaturopathyMedical devicesHaematological tumoursMedical molecular engineering of nucleic acids and proteins

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Publications (9)

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|Sep 21, 2022

Semirational bioengineering of AAV vectors with increased potency and specificity for systemic gene therapy of muscle disorders.

Jihad El Andari, Edith Renaud-Gabardos, Warut Tulalamba

|Mar 11, 2022

Disease burden and management of Crigler-Najjar syndrome: Report of a world registry.

Sem J Aronson, Norman Junge, Mediha Trabelsi

|Nov 05, 2021

Hepatic expression of GAA results in enhanced enzyme bioavailability in mice and non-human primates.

Helena Costa-Verdera, Fanny Collaud, Christopher R Riling

|Oct 27, 2021

A novel therapeutic strategy for skeletal disorders: Proof of concept of gene therapy for X-linked hypophosphatemia.

Volha V Zhukouskaya, Louisa Jauze, Séverine Charles

|Jul 02, 2021

Emerging Immunogenicity and Genotoxicity Considerations of Adeno-Associated Virus Vector Gene Therapy for Hemophilia.

Paul E Monahan, Claude Négrier, Michael Tarantino

|Feb 11, 2021

Engineering adeno-associated viral vectors to evade innate immune and inflammatory responses.

Ying Kai Chan, Sean K Wang, Colin J Chu

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Frequent Collaborators

4 joint publications

Giuseppe Ronzitti

2 joint publications

Elena Barbon

2 joint publications

Fanny Collaud

2 joint publications

Christian Leborgne

2 joint publications

Helena Costa-Verdera

1 joint publications

Peter J Lenting

1 joint publications

Dirk Grimm

1 joint publications

Daniel M Cohen

1 joint publications

Karen Huang

1 joint publications

Anna Fabiano

Frequent Collaborators

4 joint publications

Giuseppe Ronzitti

2 joint publications

Elena Barbon

2 joint publications

Fanny Collaud

2 joint publications

Christian Leborgne

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