Rachael A Potter

2PUBLICATIONS
10CO-AUTHORS
Medical virologyGenetically modified animals
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Publications (2)

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|Oct 09, 2024
AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial.

Jerry R Mendell, Francesco Muntoni, Craig M McDonald

|Sep 06, 2023
Expression and function of four AAV-based constructs for dystrophin restoration in the mdx mouse model of Duchenne muscular dystrophy.

Rachael A Potter, Danielle A Griffin, Kristin N Heller

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Frequent Collaborators

1 joint publications

Jerry R Mendell

1 joint publications

Francesco Muntoni

1 joint publications

Craig M McDonald

1 joint publications

Hirofumi Komaki

1 joint publications

Carmen Leon-Astudillo

1 joint publications

Crystal Proud

1 joint publications

Aravindhan Veerapandiyan

1 joint publications

Maitea Guridi

1 joint publications

Damon R Asher

1 joint publications

Louise R Rodino-Klapac

Frequent Collaborators

1 joint publications

Jerry R Mendell

1 joint publications

Francesco Muntoni

1 joint publications

Craig M McDonald

1 joint publications

Hirofumi Komaki

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