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Mark Walters

17PUBLICATIONS

59CO-AUTHORS

Gene and molecular therapyRecommender systemsRegenerative medicine (incl. stem cells)Tissue engineeringCardiology (incl. cardiovascular diseases)

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Publications (17)

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|Apr 27, 2026

Combinatorial base editing couples disease correction with lineage amplification in hematopoietic stem and progenitor cells.

|Apr 06, 2026

Cure Sickle Cell Initiative recommendations on common data elements for sickle cell disease gene therapy trials.

Sophie Lanzkron, Victoria H Coleman-Cowger, Alexis A Thompson

|Apr 03, 2026

CRISPR-Cas12a Gene Editing of <i>HBG1</i> and <i>HBG2</i> Promoters to Treat β-Thalassemia.

Haydar Frangoul, Rabi Hanna, Mark C Walters

|Apr 03, 2026

CRISPR-Cas12a Gene Editing of <i>HBG1</i> and <i>HBG2</i> Promoters to Treat Sickle Cell Disease.

Rabi Hanna, Haydar Frangoul, Luis Pineiro

|Mar 26, 2026

A blueprint to accelerate rare pediatric gene therapy approvals.

Mohamed Abou-El-Enein, Mark C Walters, Darshak Sanghavi

|Jan 12, 2026

Long-term efficacy and safety results of betibeglogene autotemcel gene therapy for transfusion-dependent β-thalassemia.

Janet L Kwiatkowski, Alexis A Thompson, Jennifer Schneiderman

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Frequent Collaborators

4 joint publications

Alexis Thompson

4 joint publications

Franco Locatelli

3 joint publications

Julie Washko Kanter

3 joint publications

Selim Corbacioglu

3 joint publications

Haydar Frangoul

2 joint publications

Mary Eapen

2 joint publications

Rabi Hanna

2 joint publications

Lakshmanan Krishnamurti

2 joint publications

Michael R DeBaun

2 joint publications

Akshay Sharma

Frequent Collaborators

4 joint publications

Alexis Thompson

4 joint publications

Franco Locatelli

3 joint publications

Julie Washko Kanter

3 joint publications

Selim Corbacioglu

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