Ksenija Gorni
5PUBLICATIONS
28CO-AUTHORS
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Publications (5)
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|May 11, 2024
JEWELFISH: 24-month results from an open-label study in non-treatment-naïve patients with SMA receiving treatment with risdiplam.Claudia A Chiriboga, Claudio Bruno, Tina Duong
|Oct 09, 2023
Systematic Literature Review of the Natural History of Spinal Muscular Atrophy: Motor Function, Scoliosis, and Contractures.Valerie Aponte Ribero, Yasmina Martí, Sarah Batson
|Apr 18, 2023
Correction to: Two‑year efficacy and safety of risdiplam in patients with type 2 or non‑ambulant type 3 spinal muscular atrophy (SMA).Maryam Oskoui, John W Day, Nicolas Deconinck
|Feb 03, 2023
Two-year efficacy and safety of risdiplam in patients with type 2 or non-ambulant type 3 spinal muscular atrophy (SMA).Maryam Oskoui, John W Day, Nicolas Deconinck
|Oct 18, 2021
Preferences and Utilities for Treatment Attributes in Type 2 and Non-ambulatory Type 3 Spinal Muscular Atrophy in the United Kingdom.Siu Hing Lo, Ksenija Gorni, C Simone Sutherland
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Frequent Collaborators
3 joint publications
Janbernd Kirschner
3 joint publications
Renata S Scalco
3 joint publications
Anna Kostera-Pruszczyk
3 joint publications
Paulo Fontoura
3 joint publications
Heidemarie Kletzl
3 joint publications
Eugenio Mercuri
2 joint publications
Nathalie Goemans
2 joint publications
John W Day
2 joint publications
Nicolas Deconinck
2 joint publications
Kayoko Saito
