Giuliana Ferrari

8PUBLICATIONS
46CO-AUTHORS
Medical biochemistry - inorganic elements and compoundsGene and molecular therapyHaematologyMechanobiology
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Publications (8)

|Mar 25, 2026
Iron overload damages mitochondria and induces metabolic rewiring of hematopoietic stem cells toward glycolysis.

Silvia Sighinolfi, Laura Cassina, Maria Rosa Lidonnici

|Nov 26, 2025
Base editing of β<sup>0</sup>-thalassemia mutations as a therapeutic strategy for severe β-hemoglobinopathies.

Giulia Hardouin, Pierre Martinucci, Samantha Scaramuzza

|Jul 01, 2025
Imbalanced TGFβ signalling and autophagy drive erythroid priming of hematopoietic stem cells in β-thalassemia.

Maria Rosa Lidonnici, Giulia Chianella, Nicole Mende

|Sep 07, 2023
Gene Therapy for Hemoglobinopathies.

Maria Rosa Lidonnici, Samantha Scaramuzza, Giuliana Ferrari

|May 31, 2023
Inhibition of FGF23 is a therapeutic strategy to target hematopoietic stem cell niche defects in β-thalassemia.

Annamaria Aprile, Laura Raggi, Simona Bolamperti

|Dec 12, 2022
Adenine base editor-mediated correction of the common and severe IVS1-110 (G>A) β-thalassemia mutation.

Giulia Hardouin, Panagiotis Antoniou, Pierre Martinucci

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