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Updated: Jun 6, 2025

Posterior Semicircular Canal Approach for Inner Ear Gene Delivery in Neonatal Mouse
03:52

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Published on: March 2, 2018

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对遗传性听力损失的基因治疗

Zeming Fu1, Liping Zhao2, Yingyuan Guo1

  • 1Department of Otolaryngology- Head and Neck Surgery, The Second Hospital of Jilin University, 4026 Yatai Street, Changchun 130022, China.

Hearing research
|December 1, 2024
PubMed
概括

基因疗法通过纠正基因突变,为遗传性听力损失 (HHL) 提供了希望. 腺相关病毒 (AAV) 载体在提供基因疗法方面表现有前途,在某些情况下恢复听力.

关键词:
腺相关病毒的病毒.这就是CRISPR/CasPR.基因治疗是一种基因疗法.遗传性听力损失是一种遗传性听力损失.

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