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CRISPR/Cas9 Gene Editing of Hematopoietic Stem and Progenitor Cells for Gene Therapy Applications
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Gene therapy for the Wiskott-Aldrich syndrome

Anne Galy1, Adrian J Thrasher

  • 1Inserm, U951, Molecular Immunology and Innovative Biotherapies, Genethon, Evry, France.

Current Opinion in Allergy and Clinical Immunology
|October 6, 2011
PubMed
Abstract

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