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Targeting mRNA splicing as a potential treatment for Duchenne muscular dystrophy

Ryszard Kole1, Brian J Leppert

  • 1Sarepta Therapeutics, 3450 Monte Villa Parkway, Bothell, Washington 98021, USA. RKoleAdvisor@sareptatherapeutics.com

Discovery Medicine
|August 1, 2012
PubMed

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