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A Familial Hypercholesterolemia Human Liver Chimeric Mouse Model Using Induced Pluripotent Stem Cell-derived Hepatocytes
Published on: September 15, 2018
Rosa María Sánchez-Hernández1, Pablo Prieto-Matos2, Fernando Civeira3
1Sección de Endocrinología y Nutrición, Complejo Hospitalario Universitario Insular Materno Infantil de Gran Canaria, Instituto Universitario de Investigaciones Biomédicas y Sanitarias (IUIBS) de la Universidad de Las Palmas de Gran Canaria, Las Palmas de Gran Canaria, Spain.
Autosomal recessive hypercholesterolemia (ARH) is a rare genetic disorder in Spain, characterized by high LDL-C and cardiovascular risk. This study identified a low prevalence and high genetic diversity among Spanish ARH patients.
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