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Plasma lyso-Gb3: a biomarker for monitoring fabry patients during enzyme replacement therapy

Hitoshi Sakuraba1, Tadayasu Togawa2, Takahiro Tsukimura2

  • 1Department of Clinical Genetics, Meiji Pharmaceutical University, 2-522-1 Noshio, Kiyose, Tokyo, 204-8588, Japan. sakuraba@my-pharm.ac.jp.

Clinical and Experimental Nephrology
|December 31, 2017
PubMed
Abstract

Keywords:
AntibodyEnzyme replacement therapyFabry diseaseGlobotriaosylsphingosine

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