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Precision Therapy for Inherited Retinal Disease: At the Forefront of Genomic Medicine

Nicole Koulisis1, Aaron Nagiel1

  • 1Department of Surgery, The Vision Center, Children's Hospital Los Angeles, Los Angeles, CA, USA; The Saban Research Institute, Children's Hospital Los Angeles, Los Angeles, CA, USA; USC Roski Eye Institute, Keck School of Medicine, University of Southern California, 1450 San Pablo Street, Los Angeles, CA 90033, USA.

Clinics in Laboratory Medicine
|May 23, 2020
PubMed

Keywords:
Adeno-associated virus (AAV)Clustered regularly interspaced short palindromic repeats (CRISPR)Gene transferInherited retinal diseaseNext-generation sequencing (NGS)Retinal degenerationSanger sequencingSubretinal gene therapy

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