[Current and new therapeutic options in inborn errors of metabolism]

F G Debray1,2, L Weekers1,3, C Dadoumont1,2

  • 1Unité Métabolique, Service de Génétique, CHU Liège, Belgique.

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In pediatric medicine, understanding the renal function and drug elimination nuances is crucial for administering safe and effective treatments. Newborns, in particular, display markedly slower renal functions than adults, profoundly affecting how drugs are cleared from their bodies. This slower drug clearance requires clinicians to extend the dosing intervals for many medications to prevent drug accumulation and toxicity while ensuring therapeutic efficacy.One key area where these adjustments...
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