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CRISPR-based therapeutics: current challenges and future applications

Ashley E Modell1, Donghyun Lim1, Tuan M Nguyen1

  • 1Chemical Biology and Therapeutics Science, Broad Institute of MIT and Harvard, Cambridge, MA 02142, USA; Department of Medicine, Harvard Medical School, Boston, MA 02115, USA; Divisions of Renal Medicine and Engineering, Brigham and Women's Hospital, Boston, MA 02115, USA.

Trends in Pharmacological Sciences
|December 25, 2021
PubMed

Keywords:
CRISPR-Cas9base editingcell-based therapeuticsgenome engineeringprime editing

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