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Beta-thalassemia: is cure still a dream?

Mohammad H Hodroj1, Nathalie Akiki1, Rayan Bou-Fakhredin2

  • 1Division of Hematology and Oncology, Department of Internal Medicine, American University of Beirut Medical Center, Beirut, Lebanon.

Minerva Medica
|August 3, 2023
PubMed
Summary

Beta-thalassemia, a genetic anemia disorder, presents complex clinical challenges. This review explores current and emerging treatments, including Luspatercept, to improve patient management and outcomes.

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