Molecular therapy for polyQ disorders: from bench to clinical trials

João de Sousa-Lourenço1, Ana C Silva2, Luís Pereira de Almeida3

  • 1CNC-UC - Center for Neuroscience and Cell Biology, University of Coimbra, Coimbra, Portugal; CIBB - Center for Innovative Biomedicine and Biotechnology, University of Coimbra, Coimbra, Portugal.

PubMed
Abstract