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Generation of Cationic Nanoliposomes for the Efficient Delivery of In Vitro Transcribed Messenger RNA
Published on: February 1, 2019
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Programmable lipid nanoparticle tropism unlocks precision RNA medicine
Usama Ahmad1, Robert Musiol2, Xiaojun Cai3
1Faculty of Pharmacy, Integral University, Kursi Road, Lucknow-226026, India.
Trends in Molecular Medicine
|October 18, 2025
Abstract:
Peptide-ionizable lipids (PILs) establish a rational design paradigm for RNA delivery, defining a chemical code that programs organ tropism and enables systemic prime editing. By achieving precise mRNA and genome editing beyond the liver, this platform opens a new era of multi-organ RNA therapeutics and precision genetic medicine.

