Pediatric Ataxia and Emerging Treatments

The landscape of pediatric ataxia is diverse, encompassing acute, subacute, episodic, and chronic/progressive presentations. We review the typical diagnostic strategy for chronic and progressive ataxias. We then provide an overview of emerging treatments and the pipeline for disease-modifying therapies. Unfortunately, the needle has not yet substantially shifted on survivorship in pediatric ataxia, so the focus remains on management of longer-term complications and emphasizing the importance of a multidisciplinary team and the role of palliative care.