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Updated: Aug 6, 2026

A Standard Methodology to Examine On-site Mutagenicity As a Function of Point Mutation Repair Catalyzed by CRISPR/Cas9 and SsODN in Human Cells
10:07

A Standard Methodology to Examine On-site Mutagenicity As a Function of Point Mutation Repair Catalyzed by CRISPR/Cas9 and SsODN in Human Cells

Published on: August 25, 2017

Targeted gene correction: a new strategy for molecular medicine

S Ye1, A C Cole-Strauss, B Frank

  • 1Kimeragen Inc., Newtown, PA 18940, USA.

Molecular Medicine Today
|October 30, 1998
PubMed
Summary

Gene therapy advances enable gene repair for treating genetic disorders. A novel molecular tool aims to fix mutations directly within the chromosome, heralding a new era in genetic medicine.

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