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Human Gene Therapy
|
August 4, 2010
Transgene loss and changes in the promoter methylation status as determinants for expression duration in nonviral gene transfer for factor IX
Jörg Schüttrumpf, Peter Milanov, Daniela Abriss, et al.
The FEBS Journal
|
September 18, 2008
Oxygen-induced changes in hemoglobin expression in Drosophila
Eva Gleixner, Daniela Abriss, Boris Adryan, et al.
Blood
|
October 28, 2011
Engineered factor IX variants bypass FVIII and correct hemophilia A phenotype in mice
Peter Milanov, Lacramioara Ivanciu, Daniela Abriss, et al.
Thrombosis and Haemostasis
|
November 6, 2009
Factor VIII-eGFP fusion proteins with preserved functional activity for the analysis of the early secretory pathway of factor VIII
Stefan Heinz, Jörg Schüttrumpf, Jeremy C Simpson, et al.
Plos One
|
September 14, 2012
Chemical chaperones improve protein secretion and rescue mutant factor VIII in mice with hemophilia A
Stefanie D Roth, Jörg Schüttrumpf, Peter Milanov, et al.
Human Gene Therapy. Clinical Development
|
April 18, 2018
Non-Clinical Efficacy and Safety Studies on G1XCGD, a Lentiviral Vector for Ex Vivo Gene Therapy of X-Linked Chronic Granulomatous Disease
Christian Brendel, Michael Rothe, Giorgia Santilli, et al.
Molecular Therapy. Methods & Clinical Development
|
April 18, 2020
Preclinical Evaluation of a Novel Lentiviral Vector Driving Lineage-Specific BCL11A Knockdown for Sickle Cell Gene Therapy
Christian Brendel, Olivier Negre, Michael Rothe, et al.
The New England Journal of Medicine
|
December 7, 2020
Post-Transcriptional Genetic Silencing of <i>BCL11A</i> to Treat Sickle Cell Disease
Erica B Esrick, Leslie E Lehmann, Alessandra Biffi, et al.
Biorxiv : the Preprint Server for Biology
|
June 9, 2023
Gene editing without <i>ex vivo</i> culture evades genotoxicity in human hematopoietic stem cells
Jing Zeng, My Anh Nguyen, Pengpeng Liu, et al.
Cell Stem Cell
|
December 13, 2024
Gene editing without ex vivo culture evades genotoxicity in human hematopoietic stem cells
Jing Zeng, My Anh Nguyen, Pengpeng Liu, et al.
Page
of 1
Search research articles
Search
Showing results (1-10 of 10) with videos related to
Sort By:
Page
of 1
Human Gene Therapy
|
August 4, 2010
Transgene loss and changes in the promoter methylation status as determinants for expression duration in nonviral gene transfer for factor IX
Jörg Schüttrumpf, Peter Milanov, Daniela Abriss, et al.
The FEBS Journal
|
September 18, 2008
Oxygen-induced changes in hemoglobin expression in Drosophila
Eva Gleixner, Daniela Abriss, Boris Adryan, et al.
Blood
|
October 28, 2011
Engineered factor IX variants bypass FVIII and correct hemophilia A phenotype in mice
Peter Milanov, Lacramioara Ivanciu, Daniela Abriss, et al.
Thrombosis and Haemostasis
|
November 6, 2009
Factor VIII-eGFP fusion proteins with preserved functional activity for the analysis of the early secretory pathway of factor VIII
Stefan Heinz, Jörg Schüttrumpf, Jeremy C Simpson, et al.
Plos One
|
September 14, 2012
Chemical chaperones improve protein secretion and rescue mutant factor VIII in mice with hemophilia A
Stefanie D Roth, Jörg Schüttrumpf, Peter Milanov, et al.
Human Gene Therapy. Clinical Development
|
April 18, 2018
Non-Clinical Efficacy and Safety Studies on G1XCGD, a Lentiviral Vector for Ex Vivo Gene Therapy of X-Linked Chronic Granulomatous Disease
Christian Brendel, Michael Rothe, Giorgia Santilli, et al.
Molecular Therapy. Methods & Clinical Development
|
April 18, 2020
Preclinical Evaluation of a Novel Lentiviral Vector Driving Lineage-Specific BCL11A Knockdown for Sickle Cell Gene Therapy
Christian Brendel, Olivier Negre, Michael Rothe, et al.
The New England Journal of Medicine
|
December 7, 2020
Post-Transcriptional Genetic Silencing of <i>BCL11A</i> to Treat Sickle Cell Disease
Erica B Esrick, Leslie E Lehmann, Alessandra Biffi, et al.
Biorxiv : the Preprint Server for Biology
|
June 9, 2023
Gene editing without <i>ex vivo</i> culture evades genotoxicity in human hematopoietic stem cells
Jing Zeng, My Anh Nguyen, Pengpeng Liu, et al.
Cell Stem Cell
|
December 13, 2024
Gene editing without ex vivo culture evades genotoxicity in human hematopoietic stem cells
Jing Zeng, My Anh Nguyen, Pengpeng Liu, et al.
Page
of 1