Dwight Koeberl

10PUBLICATIONS
29CO-AUTHORS
Gene and molecular therapyPharmacogenomicsIndigenous methodologiesMedical molecular engineering of nucleic acids and proteinsPredictive and prognostic markers
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Publications (10)

|Sep 08, 2026
Genome Editing for Glycogen Storage Diseases.

|Feb 02, 2026
Longitudinal characterization of Gaac.1826dupA mice reveals the cardiac, myopathic and biochemical phenotypes of Pompe disease.

Jerry F Harb, Shih-Hsin Kan, Chloe L Christensen

|Aug 02, 2024
A case study of inclusion of rural populations in research: Implications for science and health equity.

Devon Noonan, Wendy K K Lam, James Goodrich

|Apr 29, 2024
The interplay of psychosis and non-compliance with fatal outcome in an adult with MSUD.

Nadia Falah, Surekha Pendyal, Cina Sasannejad

|Sep 13, 2023
Screening data from 19 patients with late-onset Pompe disease for a phase I clinical trial of AAV8 vector-mediated gene therapy.

William B Hannah, Laura E Case, Edward C Smith

|Jul 08, 2023
Gene therapy for glycogen storage diseases.

Dwight D Koeberl, Rebecca L Koch, Jeong-A Lim

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Frequent Collaborators

2 joint publications

Raymond Y Wang

1 joint publications

Francesco Puzzo

1 joint publications

Pasqualina Colella

1 joint publications

Maria G Biferi